Kavli Affiliate: Xiang Zhang | First 5 Authors: Tianyu Pan, Xiang Zhang, Weining Shen, Ting Ye, | Summary: Gene therapies aim to address the root causes of diseases, particularly those stemming from rare genetic defects that can be life-threatening or severely debilitating. While there has been notable progress in the development of gene therapies in […]
Continue.. A Bayesian Approach for Selecting Relevant External Data (BASE): Application to a study of Long-Term Outcomes in a Hemophilia Gene Therapy Trial